Latest gene therapy News

New sickle cell disease drug approved for use in England – here’s how voxelotor works
CAR T cell therapy targeting HER2 antigen shows promise against advanced sarcoma in phase I trial
Pioneering Research Wins Prestigious EU Funding
Ride Raising Money And Awareness To Save Sight
Expanding Newborn Screening For Victorian Babies
Global Search For Missing Glaucoma Link
New company established to operate NSW’s world-leading viral vector facility
UQ health and medical research secures $10.2 million boost
CSL reports strong first half growth with immunoglobulins the highlight
Inherited retinal disease carriers need more support
How does HIV get into the cell’s centre to kickstart infection?
CAR T cell therapy for T cell lymphoma shows promise in phase I trial
A novel switch to turn genes on/off, promising step toward safer gene therapy
Research aims to transform haemophilia treatment
Centenary researchers awarded more than $2m in Ideas Grants
The Cell and Gene Catalyst call for change in submission to scope of practice review
AstraZeneca announces collaboration and investment agreement with Cellectis to accelerate cell therapy and genomic medicine ambitions
Groundbreaking gene therapy trial for Hunter syndrome opens
Dan L Duncan Comprehensive Cancer Center to open cell therapy clinical trials at Harris Health
COVID proved the therapeutic potential of RNA technology – making it more available is the next goal
Life changing gene therapy for babies with spinal muscular atrophy
Viralgen welcomes back Andy Holt as CCO
New view of gene therapy
Research: DNA shredder for gene therapy
Oculus BioMed partners with The Centre for Eye Research Australia in a deal to develop ‘SwitchGene’
CSL announces seven new Global Research Acceleration Initiative projects
Viralgen Vector Core and Elpida Therapeutics partner to manufacture gene therapy medicines for anticipated Spastic Paraplegia 50 (SPG50) and Charcot-Marie-Tooth disease type…
Next stop: retina
Alexion completes purchase and licence agreement for early-stage rare disease gene therapy portfolio from Pfizer
CSL reports strong profit growth with record plasma collections
How a cat got people talking about rare neurological diseases
Alexion, AstraZeneca Rare Disease, enters agreement with Pfizer to acquire a portfolio of preclinical rare disease gene therapies
Gene Therapy Treats Chronic Pain by Dialing Down Sodium
World first trial for kids with Duchenne Muscular Dystrophy
NSW new world first trial for kids with Duchenne Muscular Dystrophy
RNA – changing face of modern medicine
Gene therapy could help fight glaucoma: discovery
RNA offers hope for new Parkinson’s treatment
See future: Annual Review 2022
New funding to advance gene therapies
New report calls on national cell and gene therapy plan
CAR-NKT cell therapy shows promising results against neuroblastoma in phase 1 clinical trial
“Nothing short of miraculous” – The drug offering hope to MND patients
Collaborative and creative policies needed to maximize psychedelics’ therapeutic potential
Using tiny brains to treat rare, hereditary diseases
Boost for sight regenerating research
New funding boosts treatment for ultra-rare childhood dementia
Australian Cell and Gene Catalyst takes step forward